Published online Feb 6, 2019. doi: 10.12998/wjcc.v7.i3.389
Peer-review started: October 22, 2018
First decision: December 9, 2018
Revised: December 24, 2018
Accepted: December 29, 2018
Article in press: December 30, 2018
Published online: February 6, 2019
Processing time: 101 Days and 12 Hours
Gerstmann-Sträussler-Scheinker (GSS) disease is an inherited prion disease that is clinically characterized by the early onset of progressive cerebellar ataxia. The incidence of GSS is extremely low and it is particularly rare in China. Therefore, clinicians may easily confuse this disease with other diseases that also cause ataxia, resulting in its under-diagnosis or misdiagnosis.
Here, we report the first case of genetically diagnosed GSS disease in Northeast China. The patient exhibited typical ataxia and dysarthria 2.5 years after symptom onset. However, magnetic resonance imaging of the brain and spinal cord revealed a normal anatomy. Screening results for the spinocerebellar ataxia gene were also negative. We thus proposed to expand the scope of genetic screening to include over 200 mutations that can cause ataxia. A final diagnosis of GSS was presented and the patient was followed for more than 3.5 years, during which we noted imaging abnormalities. The patient gradually exhibited decorticate posturing and convulsions. We recommended administration of oral sodium valproate, which resolved the convulsions.
Patients with inherited ataxia should be considered for a diagnosis of GSS via genetic testing at an early disease stage.
Core tip: Here, we report the first case of genetically diagnosed Gerstmann-Sträussler-Scheinker (GSS) in Northeast China. A 3.5-year follow-up period provided particularly interesting insights into the disease course and its associated imaging findings. The variable symptoms and diagnostic methods used for this disease are also discussed in depth with reference to the current case and several previous cases. Since GSS is particularly rare in China, it may be easily misdiagnosed. This case may contribute to improving our understanding and diagnosis of GSS.