Published online Oct 15, 2022. doi: 10.4251/wjgo.v14.i10.2061
Peer-review started: June 8, 2022
First decision: August 20, 2022
Revised: September 4, 2022
Accepted: September 13, 2022
Article in press: September 13, 2022
Published online: October 15, 2022
Processing time: 127 Days and 20.6 Hours
The prognosis of patients with advanced biliary tract cancer (BTC) is poor. The clinical efficacy of combining chemotherapy (CT) with targeted therapy (TT) as first-line treatment remains controversial.
Currently, TT based on actionable genetic alterations in BTC are being extensively explored. However, the clinical efficacy of combination CT with TT as first-line treatment for advanced BTC is unclear. A meta-analysis is necessary to systematically and comprehensively evaluate the clinical value of TT for advanced BTC.
The purpose of this meta-analysis was to explore the value of CT combined with TT as first-line treatment for advanced BTC.
We systematically searched PubMed, EMBASE, ClinicalTrials, Scopus, and the Cochrane Library databases to screen and include randomized clinical trials (RCTs) on gemcitabine-based CT alone vs the combination of TT and CT as first-line treatment for advanced BTC. Review Manager 5.4.1 software was used to conduct the statistical analysis. Objective response rate (ORR), progression-free survival (PFS) and overall survival (OS) were analyzed as main outcomes. Subgroup analyses based on different targeted agents, CT regimens and tumor locations were performed.
Our meta-analysis showed a significant improvement in ORR in patients treated with CT + TT compared to those treated with CT alone (P = 0.007), but no difference in PFS or OS. Similar trends were observed in the subgroup treated with agents targeting EGFR (P = 0.004). Notably, patients who received a CT regimen of gemcitabine + oxaliplatin in the CT + TT arm had both a higher ORR (P = 0.004) and longer PFS (P = 0.03) than those in the CT-only arm. Moreover, patients with cholangiocarcinoma treated with CT + TT had significantly increased ORR and PFS.
Our study is the first meta-analysis of RCTs to evaluate the efficacy of the combining TT with standard CT as first-line treatment for advanced BTC. The meta-analysis has demonstrated that CT + TT is a promising first-line treatment for advanced BTC that leads to improved clinical outcomes.
In the future, more clinical studies are needed to explore the role of TT for advanced BTC. In addition, attention should be paid on the interactions of CT regimen and tumor location for assessing the clinical efficacy of TT in advanced BTC.