Published online Jul 28, 2023. doi: 10.3748/wjg.v29.i28.4416
Peer-review started: February 23, 2023
First decision: May 16, 2023
Revised: June 5, 2023
Accepted: July 5, 2023
Article in press: July 5, 2023
Published online: July 28, 2023
Processing time: 153 Days and 3.4 Hours
The association between diabetes mellitus (DM) and cholangiocarcinoma (CCA) progression has been established with unclear mechanisms. Our previous study showed that γ-aminobutyric acid B2 receptor (GABBR2) is among the top 5 upregulated genes in CCA cells cultured in high glucose (HG). Thus, GABBR2 is highly potential for a repurposing aim in CCA treatment.
Approximately 60% of Thai patients with CCA had fasting blood glucose in a range of pre-diabetes or DM. Targeting the molecules underlying hyperglycemia-induced aggressiveness of CCA cells might improve the prognosis of CCA patients with DM.
This study aimed to investigate the effects of hyperglycemia on GABBR2 expression and the potential use of GABBR2 as a CCA therapeutic target.
CCA cells cultured in normal glucose or HG conditions were used as models of in vitro euglycemia and hyperglycemia, respectively. Baclofen, a GABBR2 agonist, was used to study the functional roles of CCA cells. Western blot, immunocytofluorescence, and immunohistochemistry were used to study molecular mechanisms.
HG induced GABBR2 expression in both cell lines and in patients’ CCA tissues. Baclofen treatment significantly suppressed CCA cell growth, while cells cultured in HG showed a significantly higher sensitivity. The effects of baclofen on CCA cell growth were achieved by the suppression of the signal transducer and activator of transcription 3 and glycogen synthase kinase 3/β-catenin pathways.
The expression of GABBR2 in CCA is induced in hyperglycemic conditions. Baclofen significantly suppresses the growth of CCA cells and thus holds a high promise as a repurposing drug for CCA treatment.
Investigating baclofen’s effects at an optimal therapeutic dosage in in vivo models would verify the present work and facilitate the translation for clinical study in CCA cases.